F075 From Blisters to Breakthroughs: Updates in Epidermolysis Bullosa
DESCRIPTION
Open admission to eligible categories, no tuition or ticket
Join our session to learn essential care practices for epidermolysis bullosa (EB) patients, including optimizing care for newborns with EB. Explore newly FDA-approved treatments and treatments in the pipeline, such as topical gene therapy, gene therapy grafts, and anti-inflammatory treatments. Hear firsthand from an EB parent about their experiences with these innovative treatments and living with EB. Gain invaluable insights to enhance your care for EB patients in your practice.
LEARNING OBJECTIVES
Describe the types of Epidermolysis Bullosa (EB) and their management
Assess novel therapies for epidermolysis bullosa and appropriate scenarios for use.
Appreciate the patient perspective of living with epidermolysis bullosa
SPEAKERS
Maria Gnarra Buethe, MD, PhD, FAAD
Heather Fullmer
Emily S Gorell, DO, MS, FAAD
Laura Levin, MD, FAAD
M. Peter Marinkovich, MD, FAAD
Dedee F. Murrell, MD, FAAD
Amy S. Paller, MD, FAAD
HANDOUTS
SPEAKER DISCLOSURES
Maria Gnarra Buethe, MD, PhD, FAAD
No financial relationships exist with ineligible companies.
Heather Fullmer
No financial relationships exist with ineligible companies.
Emily S Gorell, DO, MS, FAAD
Abeona Therapeutics – Advisory Board(Honoraria), Consultant (1099 relationship)(Fees); Amryt Pharma – Advisory Board(Honoraria); Chiesi – Advisory Board(Honoraria); Krystal Biotech, Inc – Advisory Board(Honoraria), Consultant(Honoraria);
Laura Levin, MD, FAAD
No financial relationships exist with ineligible companies.
M. Peter Marinkovich, MD, FAAD
No financial relationships exist with ineligible companies.
Dedee F. Murrell, MD, FAAD
Abbott Laboratories – Advisory Board(Honoraria), Speaker(Honoraria); AbbVie – Investigator(Grants/Research Funding); Actavis – Speaker/Faculty Education(Honoraria); Almirall – Consultant(Honoraria); Amgen – Investigator(Fees); Amicus Therapeutics – Advisory Board(Honoraria); Amryt Pharma – Investigator(Fees); Anacor Pharmaceuticals, Inc. – Investigator(Grants/Research Funding); Arena Pharmaceuticals – Investigator(Grants/Research Funding); arGEN-X – Investigator(Fees); Ascent Pharmaceuticals – Speaker(Honoraria); Castle Creek Pharmaceuticals – Consultant(Fees); Chiesi Farmaceutici – Advisory Board(Fees); CSL – Speaker(Grants/Research Funding), Speaker(Honoraria); Delfin Technology – Investigator(Equipment); Eli Lilly and Company – Advisory Board(Honoraria); Galderma Laboratories, L.P. – Investigator(Grants/Research Funding), Investigator(Other Financial Benefit); Janssen-Ortho Inc. – Other(Grants/Research Funding); Leo Pharma Inc – Speaker/Faculty Education(Honoraria); Medimmune – Investigator(Grants/Research Funding); Merck Serono – Investigator(Fees), Investigator(Grants/Research Funding); Molynlycke – Speaker(Grants/Research Funding); Novartis Pharmaceuticals Corp. – Advisory Board(Honoraria), Investigator(Grants/Research Funding); Pfizer Inc. – Investigator(Grants/Research Funding); Pierre Fabre Dermo-Cosmétique US – Speaker(Honoraria); Principia Biopharma Inc – Consultant(Honoraria); Roche Laboratories – Advisory Board(Honoraria), Investigator(Grants/Research Funding); Samumed, LLC – Investigator(Grants/Research Funding); Sanofi – Advisory Board(Fees), Investigator(Fees), Investigator(Grants/Research Funding); Schering-Plough Corporation – Investigator(Grants/Research Funding), Speaker(Other Financial Benefit); Shire – Advisory Board(Honoraria), Investigator(Grants/Research Funding); Stiefel a GSK company – Speaker(Honoraria); XOMA (US) LLC – Investigator(Grants/Research Funding);
Amy S. Paller, MD, FAAD
AbbVie – Data Safety Monitoring Board(Honoraria), Investigator(Grants/Research Funding); Abeona Therapeutics – Data Safety Monitoring Board(Honoraria); Arcutis Biotherapeutics – Consultant (1099 relationship)(Honoraria); BioCryst Pharmaceuticals, Inc. – Consultant (1099 relationship)(Honoraria), Data Safety Monitoring Board(Honoraria); BioMendics, LLC – Investigator(Grants/Research Funding); Boehringer Ingelheim – Consultant(Honoraria); Castle Creek Pharmaceuticals – Consultant (1099 relationship)(Honoraria); Chiesi Farmaceutici – Consultant (1099 relationship)(Honoraria); Daiichi Sankyo – Data Safety Monitoring Board(Honoraria); Dermavant Sciences, Inc. – Investigator(Grants/Research Funding); Eli Lilly – Consultant (1099 relationship)(Honoraria), Investigator(Grants/Research Funding); Galderma – Data Safety Monitoring Board(Honoraria); Incyte Corporation – Investigator(Grants/Research Funding); Johnson & Johnson Innovative Medicine – Consultant (1099 relationship)(Honoraria), Investigator(Grants/Research Funding); Krystal Biotech, Inc – Consultant(Honoraria); L'Oréal France – Consultant (1099 relationship)(Honoraria); Leo Pharma Inc – Consultant(Honoraria); MoonLake Immunotherapeutics – Consultant (1099 relationship)(Honoraria); Pelthos Therapeutics – Consultant (1099 relationship)(Honoraria); Quoin Pharmaceuticals Ltd – Consultant (1099 relationship)(Honoraria); Regeneron – Consultant(Honoraria), Investigator(Grants/Research Funding); Sanofi Genzyme – Consultant(Honoraria); UCB – Investigator(Grants/Research Funding);